The first study assessing the real-world commercial roll-out of gene therapies for sickle cell disease and beta thalassemia offers lessons learned to inform best practices as manufacturers and medical centers prepare to meet growing demand for gene therapies in the coming years. Read more
Medical News - Dec 07
Patients who underwent hematopoietic cell transplantation for sickle cell disease saw high rates of survival without disease symptoms and low rates of severe side effects or complications years after their procedure, according to a new study. Read more
Medical News - Dec 07
Preliminary results from two trials of the gene therapy exagamglogene autotemcel (exa-cel) suggest the therapy offers an effective cure for beta-thalassemia and sickle cell disease in children younger than 12. Read more
Medical News - Dec 06
Central Florida’s Sickle Cell Conquerors hosted their first-ever Sickle Cell Walk at Carver Middle School in Orlando. Read more
Yahoo! News - Sep 14
Everything you need to know about sickle cell disease Read more
Evening Standard - Sep 03
